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Tagged: Mitochondrial

Recent Advance of Gene Therapy in Rare Diseases

May 13th, 2021 | Mitochondrial

Gene Therapy improved vision in patients with leber hereditary optic neuropathy (LHON) By: Dr. Maria Niu Mitochondria, powerhouses of eukaryotic cells, is a certain kind of cytoplasmic organelle and plays a critical role in energy production. Mitochondria dysfunction results in a broad spectrum of multisystem disorders. LHON is a mitochondrial neurodegenerative disease typically caused by […]

Mitochondrial Diseases and the Challenges of Clinical Trials

August 22nd, 2019 | Mitochondrial

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