How we can help The BBCR team provides knowledge in cell, biologics and gene therapies BBCR addresses sponsors’ questions in the ever-changing regulatory environment We offer clinical strategy for orphan diseases and precision medicine RWE can be used to build orphan diseases evidence to support regulatory decisions BBCR serves small and medium sized Biotech Companies, […]
Tagged: Gene Therapies
The BBCR mission is to customize strategies, simplify clinical research, design cost-effective trials, streamline protocols, and create a regulatory roadmap. Learn more about our services by visiting bbcrconsulting.com
September 20th, 2022 | Gene Therapies2019 Successful Clinical Plan and Drug Development Stories
January 27th, 2020 | Gene Therapies
Gene therapies for disorders such as X-linked Severe Combined Immunodeficiency (SCID, sometimes known as “bubble boy disease”), and Spinal Muscular Atrophy (SMA) have, for the first time, shown remarkable safety and efficacy results in clinical trials. FDA approved Trikafta, a gene-based therapy creating hope for children with cystic fibrosis and Zolgensma, a gene therapy drug, […]
Potential Clinical Plans for Gene Therapies in Rare Disorders
January 9th, 2020 | Gene Therapies
BBCR Consulting, for the first time this year, decided to attend the European edition of the Gene Therapies in Rare Disorders conference in London UK. In our opinion, the event, as promised, proved to be: ”…uniquely focused conference that will bring the leaders in the field together to discuss the critical factors involved in driving […]
Potential of Gene Therapies in Rare Disorders
November 12th, 2019 | Gene Therapies
BBCR Consulting, for the first time this year, decided to attend on October 15th – 17th in London- UK, the European edition of the Gene Therapies in Rare Disorders conference. In our opinion, the event, as promised, proven to be: ”…uniquely focused conference that will bring the leaders in the field together to discuss the […]